Social media platforms and podcasts are spotlighting the untold stories of rare disease patients and their families. Find out more in today's Few & Far Between podcast episode. Biorasi's Becky Knockemus welcomes guests Effie Parks, host of the Once Upon a Gene podcast, and Špela Miroševič, co-founder and president of the CTNNB1 Foundation.
Welcome to Few & Far Between: Conversations About Rare Disease Research with your host, Chris O'Brien. Episode Zero contains everything you need to know...
“Our studies are open for those that have exhausted standard of care, and we're showing improved responses, and the data is promising. So, I...
"The history of rare disease drug development indicates that once you start looking harder for cases, you often tend to find them." - Will...